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In Vivo Silencing of Regulatory Elements Using a Single AAV-CRISPRi Vector

  • P. Laurette
  • , C. Cao
  • , D. Ramanujam
  • , M. Schwaderer
  • , T. Lueneburg
  • , S. Kuss
  • , L. Weiss
  • , R. Dilshat
  • , E. E.M. Furlong
  • , F. Rezende
  • , S. Engelhardt
  • , R. Gilsbach
  • University Hospital Heidelberg
  • Partner Site Munich Heart Alliance
  • DZHK Partner Site Rhein/Main
  • Johann Wolfgang Goethe University
  • Technical University of Munich
  • University of Freiburg
  • European Molecular Biology Laboratory Heidelberg

Research output: Contribution to journalArticlepeer-review

6 Scopus citations
Original languageEnglish
Pages (from-to)223-225
Number of pages3
JournalCirculation Research
Volume134
Issue number2
DOIs
StatePublished - 19 Jan 2024

Keywords

  • epigenetic repression
  • gene editing
  • gene silencing
  • genetic therapy
  • genomics

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